We can save families from unnecessary suffering and financial hardship. We can give children more years of quality life.

Late last year, the therapy developers dosed their first patient following positive preclinical data demonstrating safety and ...

A devastating disease that's rare, fatal, and until now untreatable. How a new therapy may give kids a better life.

MEDFORD, Ore.- A fundraiser held at the Children’s Museum of Southern Oregon raises thousands of dollars to help a local boy ...

At age 2, Cal Carr was already reaching developmental milestones later than expected — and then she started regressing.

Duchenne muscular dystrophy (DMD) in India faces challenges in diagnosis, treatment, and support, highlighting the urgent ...

A Tucson preschool teacher spotted a developmental quirk in a little boy who was then able to get early treatment for ...

Pediatrics and Medicine, School of Medicine, and the Department of Physical Education, University of California, Los Angeles. Supported in part by grants from the Muscular Dystrophy Associations ...

The symposium took place on 18 th March 2025, as part of the Muscular Dystrophy Association (MDA) Clinical & Scientific ...

The golf tournament is raising funds for Vanderbilt University Medical Center’s Camp Hope and the Muscular Dystrophy Association. Camp Hope is a nonprofit organization that offers children ...